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Preclinical evaluation of tissue-selective gene therapies for congenital generalised lipodystrophy

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Tiwari, M, Roumane, A, Sommer, N, Han, W, Delibegovic, M, Rochford, J & McIlroy, G D 2024, 'Preclinical evaluation of tissue-selective gene therapies for congenital generalised lipodystrophy', Gene Therapy, vol. 31, pp. 445–454. https://doi.org/10.1038/s41434-024-00471-z

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