Myeloid/Microglial driven autologous hematopoietic stem cell gene therapy corrects a neuronopathic lysosomal disease

Sergijenko, A, Langford-Smith, A, Liao, A Y, Pickford, C E, McDermott, J, Nowinski, G, Langford-Smith, K J, Merry, C L R, Jones, S A, Wraith, J E, Wynn, R F, Wilkinson, F L & Bigger, B W 2013, 'Myeloid/Microglial driven autologous hematopoietic stem cell gene therapy corrects a neuronopathic lysosomal disease', Molecular therapy : the journal of the American Society of Gene Therapy, vol. 21, no. 10, pp. 1938-49. https://doi.org/10.1038/mt.2013.141