Systemic restoration of UBA1 ameliorates disease in spinal muscular atrophy
Date
2016-07-21
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Powis, R A, Karyka, E, Boyd, P, Come, J, Jones, R A, Zheng, Y, Szunyogova, E, Groen, E J N, Hunter, G, Thomson, D, Wishart, T M, Becker, C G, Parson, S H, Martinat, C, Azzouz, M & Gillingwater, T H 2016, 'Systemic restoration of UBA1 ameliorates disease in spinal muscular atrophy', JCI Insight, vol. 1, no. 11, e87908. https://doi.org/10.1172/jci.insight.87908